KJ Muldoon — who was diagnosed with CPS1 deficiency at one week old — received the first-ever custom gene-editing infusion to ...

Kaddis said insurers are locked in a cat-and-mouse game with drugmakers as the insurance sector invests in biosimilars and ...

This week a group of researchers, bioethicists, publishers and theologians are discussing the merits of human heritable genome editing.

While the medical world is melting down from the absolute apocalypse that is RFK Jr., it's good to celebrate that (at least ...

Alfred E. Mann Charities has made a generous gift of $12 million to establish the Alfred E. Mann Cell and Gene Therapy ...

For 21-year-old Javarian Weatherspoon, life without pain feels like a miracle. After growing up with sickle cell disease, he ...

A program offering comprehensive primary and specialist care for adults with SCD reduced visits to the emergency department, ...

CRISPR Therapeutics CRSP announced that it has entered into a collaboration deal with San Diego-based privately held company, ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene-editing treatment made just for him. Researchers described the case in a new study, say ...

In the Phase 2 study of patients with chronic kidney disease, the highest dose of the drug lowered by 86% the levels of ...

A favorable appeals court ruling repositioned a coalition of universities and Nobel laureates to win credit for inventing a ...

CRISPR Therapeutics is still losing money, but it also finished March with $1.9 billion in cash after burning through $134 ...